Biomarin Pharmaceutical

Filed a patent for "compositions and methods for treating stxbp1 disorders" on Mon, April 24, 2023

Filed a patent for "methods of treating anti-aav seropositive hemophilia patients" on Mon, May 15, 2023

Filed a patent for "high throughput screen for genetic variants associated with short stature" on Wed, June 7, 2023

Filed a patent for "epigenetic modifiers improve aav gene therapy durability" on Tue, September 12, 2023

Filed a patent for "high throughput screen for genetic variants associated with short stature" on Wed, September 27, 2023

Filed a patent for "high throughput screen for genetic variants associated with short stature" on Tue, March 12, 2024

Filed a patent for "large scale adeno-associated virus production systems" on Fri, January 26, 2024

Filed a patent for "dystrophin exon skipping oligonucleotides" on Fri, May 5, 2023

Filed a patent for "dystrophin exon skipping oligonucleotides" on Tue, January 23, 2024

Filed a patent for "targeted therapeutic lysosomal enzyme fusion proteins, associated formulations and uses thereof" on Thu, August 8, 2024

Filed a patent for "compositions and methods for treating long qt syndrome" on Fri, September 2, 2022

Filed a patent for "cnp therapy" on Fri, October 21, 2022

Filed a patent for "novel adeno-associated virus capsid proteins" on Thu, October 12, 2023

Filed a patent for "method of treating duchenne muscular dystrophy" on Fri, December 16, 2022

Filed a patent for "use of c-type natriuretic peptide variants to treat skeletal dysplasia" on Thu, September 21, 2023

Filed a patent for "process for enriching adeno-associated virus" on Thu, December 21, 2023

Filed a patent for "aav production systems for aav viral particles with improved infectivity" on Thu, April 18, 2024

Filed a patent for "use of histidine rich peptides as a transfection reagent for raav and rbv production" on Thu, April 25, 2024

Filed a patent for "treatment of cardiomyopathy with aav gene therapy vectors" on Wed, August 16, 2023

Filed a patent for "treatment of arrhythmogenic cardiomyopathy with aav gene therapy vectors" on Mon, September 11, 2023

Filed a patent for "methods of redosing gene therapy vectors" on Thu, June 20, 2024

Filed a patent for "use of c-type natriuretic peptide variants to treat skeletal dysplasia" on Thu, May 16, 2024

Filed a patent for "gene therapy vector constructs and methods of use" on Thu, September 22, 2022

Filed a patent for "treatment of arrhythemogenic cardiomyopathy with aav gene therapy vectors" on Thu, September 22, 2022

Filed a patent for "treatment of cardiomyopathy with aav gene therapy vectors" on Thu, September 22, 2022